Sight Restored: Gene Therapy Breakthrough Wins Major Science Prize

1 min read
Source: The Guardian
Sight Restored: Gene Therapy Breakthrough Wins Major Science Prize
Photo: The Guardian
TL;DR

A married couple and investigator Katherine High share a $3 million Breakthrough Prize for Luxturna, the gene therapy approved in 2017 that restores vision in people with Leber congenital amaurosis by delivering a working RPE65 gene to retinal cells; the 25-year project produced dramatic patient improvements and was celebrated at a Los Angeles ceremony, while scientists warned about politicized attacks on science and other prize-winning work highlighted advances in gene therapies for blood disorders.

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