Breakthrough in Huntington’s Disease Treatment with Successful Gene Therapy Trials
TL;DR
An experimental gene therapy called AMT-130 from Uniqure significantly slowed Huntington's disease progression by 75% over three years, potentially paving the way for the first genetic treatment approval for this neurodegenerative disorder.
- Experimental gene therapy for Huntington’s markedly slowed disease progression in key trial statnews.com
- Huntington's disease successfully treated for first time BBC
- A clever genetic technique may treat a horrible brain condition The Economist
- Huntington’s disease treated successfully for first time in UK gene therapy trial The Guardian
- UniQure ‘Exceeds Expectations’ in Much-Anticipated 3-Year Huntington’s Readout BioSpace
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