FDA Approves Sarepta Therapeutics' Gene Therapy for Duchenne Muscular Dystrophy.

TL;DR
The FDA has approved Sarepta Therapeutics' gene therapy treatment for children with Duchenne muscular dystrophy, despite questions about its clinical benefit.
Topics:businesshealthcare#clinical-benefit#duchenne-muscular-dystrophy#fda#gene-therapy#healthcare#sarepta-therapeutics
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