All articles tagged with #angelman syndrome
Annie Morgan’s days caring for Ava, who has Angelman syndrome, reveal the mounting emotional and physical toll of long-term caregiving, amplified by a patchwork of support as the U.S. shifts toward family-centered care.
Yale researchers secured a $40M NIH grant to advance STEP, a 10-nm brain-delivery platform for CRISPR gene editors; early preclinical work in mice hints at brain-wide delivery and functional gains, but the mechanism remains unclear, safety and scaling concerns persist, and full details won’t be published until 2028 as clinical work progresses.